Title | : | Investigational Therapy For Duchenne Muscular Dystrophy |
Duration | : | 7 minutes, 56 seconds |
Uploader | : | CheckRare |
Added On: | : | 18 March, 2024 |
Views | : | 368 times |
Likes | : | 0 |
Source | : | YouTube |
Matt Trudeau, head of ITF Therapeutics, discusses givinostat, an investigational therapy for Duchenne muscular dystrophy (DMD).DMD is a rare neuromuscular disease caused by genetic variants in the DMD gene. The disease primarily affects the muscles, leadi